mRNA-based therapy in a rabbit model of variegate porphyria offers new insights into the pathogenesis of acute attacks
Keywords:
mRNA delivery
Lipid nanoparticles
Rare metabolic disease
Hepatic heme synthesis
Pharmacological model of variegate porphyria
Characterization of variegate porphyria rabbits
Editorial note:
© 2021 The Author(s)
Citation:
Fontanellas-Romá, A. (Antonio); Martini, P. (Paolo); Gouya, L. (Laurent); et al. "mRNA-based therapy in a rabbit model of variegate porphyria offers new insights into the pathogenesis of acute attacks". Molecular Therapy Nucleic Acids. 25, 2021, 207 - 219
Statistics and impact
0 citas en
0 citas en
Items in Dadun are protected by copyright, with all rights reserved, unless otherwise indicated.